rare_disease

The latest news about rare_disease: headlines, AI summaries and the full story from every source.

• BioMarin Reports Positive Five-Year Data for Pompe Disease Combination Therapy CNBC · October 2, 2026, 16:18 UTC
• New ICD-10-CM Code for Glanzmann Thrombasthenia Secured Through Advocacy PR Newswire · October 1, 2026, 14:10 UTC
• Omeros Gains as AstraZeneca's Ultomiris Fails in Rare Blood Disorder Trial Seeking Alpha · July 27, 2026, 16:03 UTC